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Vutrisiran (hereditary transthyretin-mediated amyloidosis with polyneuropathy (stage 1 or 2))
Subject:
- Active Substance: Vutrisiran
- Name: Amvuttra®
- Therapeutic area: Hereditary transthyretin-mediated amyloidosis
- Pharmaceutical company: Alnylam Germany GmbH
Time table:
- Start: 15.10.2022
- Publication of assessment: 16.01.2023
- End of public hearing: 06.02.2023
- Final decision by G-BA: beginning of April 2023
Comparative therapy:
- Tafamidis (only for hATTR-PN stadium 1) or patisiran