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Cerliponase alfa (re-assessment: neuronal ceroid lipofuscinosis type 2 (CLN2 disease))

 

Subject:

  • Active Substance: Cerliponase alfa
  • Name: Brineura®
  • Therapeutic area: Neuronal ceroid lipofuscinosis type 2 (CLN2 disease)
  • Pharmaceutical company: BioMarin Deutschland GmbH

 

Time table:

  • Start: 01.07.2022
  • Final decision by G-BA: 15.12.2022

 

Final decision:

  • HInt for a major additional benefit